Sci. adv. Sci. adv. Gene therapy with AR isoform 2 rescues spinal and bulbar muscular atrophy phenotype by modulating AR transcriptional activity Lim Wooi F Forouhan Mitra Roberts Thomas C Dabney Jesse Ellerington Ruth Speciale Alfina A Manzano Raquel Universidad de Zaragoza Lieto Maria Sangha Gavinda Banerjee Subhashis Conceição Mariana Cravo Lara Biscans Annabelle Roux Loïc Pourshafie Naemeh Grunseich Christopher Duguez Stephanie Khvorova Anastasia Pennuto Maria Cortes Constanza J La Spada Albert R Fischbeck Kenneth H Wood Matthew JA Rinaldi Carlo 2021 research-article